Publications
4 July 2023

BG04 Oleogel-S10 (birch triterpenes) in the treatment of epidermolysis bullosa wounds: 24-month efficacy and safety data from the EASE study

Keywords: Oleogel-S10, Amryt, Abstract
4 July 2023

Il finanziamento della ricerca clinica in Advanced Therapy Medicinal Products (ATMP): cosa determina l’intervento dellaFinanza?

Keywords: finanza, gap di finanziamento, ATMP, terapie avanzate, ricerca medica, studi clinici, PMI
4 July 2023

Overview of patients’ cohorts in the French National rare disease registry

Keywords: Rare disease national registry, Fnaace
7 July 2023

Heterogeneity of reported outcomes in epidermolysis bullosa clinical research: a scoping review as a first step towards outcome harmonization

Br J Dermatol. 2023 Jul 7;189(1):80-90. doi: 10.1093/bjd/ljad077. PMID: 37098154. Heterogeneity of reported outcomes in epidermolysis bullosa clinical research: a scoping review as a first step […]
7 July 2023

Epidermolysis bullosa: time to come together for better outcomes

Br J Dermatol. 2023 Jul 7;189(1):5. doi: 10.1093/bjd/ljad123. PMID: 37067920. Epidermolysis bullosa: time to come together for better outcomes Authors: Gabriela Petrof 1, Anna E Martinez 1 Affiliation: Abstract: […]
11 August 2023

Safety and efficacy of autologous melanocyte/keratinocyte transplantation in patients with refractory stable vitiligo

Dermatology. 2023 Aug 11. doi: 10.1159/000533353. Epub ahead of print. PMID: 37573775. Safety and efficacy of autologous melanocyte/keratinocyte transplantation in patients with refractory stable vitiligo Authors: […]
18 August 2023

Airway stem cell reconstitution by the transplantation of primary or pluripotent stem cell-derived basal cells

Cell Stem Cell. 2023 Aug 18;S1934-5909(23)00281-3. doi: 10.1016/j.stem.2023.07.014. Online ahead of print. PMID: 37625411. Airway stem cell reconstitution by the transplantation of primary or pluripotent stem cell-derived basal […]
25 August 2023

Realising the potential of gene therapies for rare and ultra-rare inherited diseases

 Hum Gene Ther. 2023 Aug 25. doi: 10.1089/hum.2023.127. Epub ahead of print. PMID: 37624746. Realising the potential of gene therapies for rare and ultra-rare inherited diseases […]
29 August 2023

Painting and dissecting Epidermolysis Bullosa Simplex-associated keratin aggregates

Journal of Dermatological Science, Pre-proof, 2023 August 29, https://doi.org/10.1016/j.jdermsci.2023.08.007 Painting and dissecting Epidermolysis Bullosa Simplex-associated keratin aggregates Authors: Katrin Rietscher1, Melanie Homberg1, Ilya Kovalenko2,3,4,5, Jonathan Z. […]