FAI VOLARE LA RICERCA E LA CURA!
+39 345 2601842
info@lealidicamilla.org
Advanced Therapies
Cell Therapy
Gene Therapy
ATMPS
Cell & Molecular Biology
Cell & Molecular Biology
Skin Cancer
Clinical Management
EB Clinical Management
Ophthalmology
Patient Engagement
Rare Diseases
English
Dona ora
✕
Gene editing
Filtra per
Categorie
Tags
Autori
Mostra tutto
Tutto
ATMPS
Cell & Molecular Biology
Cell Therapy
EB Clinical Management
Gene Therapy
Guidelines
Ophthalmology
Patient engagement
Publications
Rare Diseases
Skin Cancer
Tutto
3D cell culture
3D printing
ABCB5
Abstract
Airway
Amryt
Anesthesia
Aniridia
ATMPs
B-VEC
Carcinogenesis
Clinical management
Clinical manifestations
Clinical trial
Coding
Cornea
Dematology
dupilumab
EB
EB epidemiology
EBS
Empowerment
Endpoints
Epidermis
Epithelial tissue homeostasis
Fibroblasts
Fibrosis
Finanza
gastrointestinal complications of EB
Gene editing
Gene therapy
genetics
genodermatosis
Guideline
Ichhtiosys
Infection-bacterial
Inflammation
Integrin α3β1
IPSc
itch
JEB
Krystal
Losartan
LSCD
Mesenchymal stromal cells
NGS
Oleogel S10
Ophthalmology
ORPHAcodes
Orphan Drug
Outcome measurement
p63
Palliative care
Parental Intervention
Pathophisiology
Patient engagement
PAX6
Personalized care
Pharmacovigilance
Pseudomonas aeruginosa
Rare Diseases
RD registry
RDEB
Review
School
self-renewal
Single-cell analysis
Skin cancer
skin cancer pathogenesis
Specialist centre
Tissue engineering
Trametinib
Unproven cell therapies
Wound healing
Tutto
Le ali di Camilla
29 May 2021
A non-viral and selection-free COL7A1 HDR approach with improved safety profile for dystrophic epidermolysis bullosa
Mol Ther Nucleic Acids. 2021 May 29;25:237-250. doi: 10.1016/j.omtn.2021.05.015. PMID: 34458008; PMCID: PMC8368800. A non-viral and selection-free COL7A1 HDR approach with improved safety profile for dystrophic epidermolysis bullosa
[…]
11 April 2023
A Review of CRISPR-Based Advances in Dermatological Diseases
Mol Diagn Ther. 2023 Jul;27(4):445-456. doi: 10.1007/s40291-023-00642-5. Epub 2023 Apr 11. PMID: 37041404. A Review of CRISPR-Based Advances in Dermatological Diseases Authors: Lu X, Jin H.
[…]
20 June 2023
Gene editing with ‘pencil’ rather than ‘scissors’ in human pluripotent stem cells
Keywords: Human pluripotent stem cells, Disease modeling, Ex vivo therapy, Isogenic pair, Base editors, Prime editor, Base substitution, Cas9
11 October 2023
CRISPR/Cas9 Based Non-viral Gene Editing Therapy for Topical Treatment ofRecessive Dystrophic Epidermolysis Bullosa
Molecular Therapy: Methods & Clinical Development – JOURNAL PRE-PROOF CRISPR/Cas9 Based Non-viral Gene Editing Therapy for Topical Treatment ofRecessive Dystrophic Epidermolysis Bullosa Authors: Xianqing Wang, Xi
[…]
